Cystic fibrosis impacts have been changing fast the past 2 decades.  CF modulators have transformed life expectancy and daily health for many people with CF. Modulators only work if the CFTR protein is made correctly, which means they help people with “folding” or “gating” mutations — not those whose gene never makes a usable protein at all.

These Nonsense/stop mutations shut the protein down at the blueprint stage, so modulators have nothing to “fix. This leaves people like our 21‑year‑old daughter, Julia,  fighting CF with grit, discipline, and treatments that manage symptoms rather than correct the root cause.

The progress is real, thanks to people like you who have personally funded it. It’s incomplete until therapies exist for every mutation, including nonsense mutation for those with CF like Julia.

Families like ours are asking for continued research, funding, and urgency so that the breakthroughs others celebrate can finally reach the people still waiting. 

Thank you for your continued support which is truly making a difference in those like Julia that fight CF.  Thank you for the consideration of donating.  

#TEAM4JB
#FUCF