There is still no cure for cystic fibrosis for those with rare and nonsense mutations like Zachary’s (G542X). Our goal is to help change that reality.
 

Cystic fibrosis is a genetic, life-shortening disease that affects the lungs, pancreas, and other vital organs, making it difficult to breathe and fight infections. While meaningful progress has been made, too many individuals are still waiting for treatments that work for their specific mutation.
 

This year brings encouraging news for Zachary. His lung function has improved significantly—from the low 70s to the low 90s—and he continues to stay committed to his daily care. After participating in a clinical trial last summer with Arcturus, he has now been accepted into a new mRNA study (RCT2100) this summer, offering continued hope for breakthrough treatments.
 

Every step forward matters, but there is still more work to be done.
 

Will you help us find a cure for everyone living with cystic fibrosis?
 

By supporting our fundraising efforts, you are helping advance the research and innovation needed to make that goal a reality.